Medicine’s ‘Wild West’? Why an advocate for those with rare diseases opposes right-to-try

These drugs are highly needed. Nobody understands this better than I do. I still walk into my son’s room every single night to see if he’s still breathing. But Special Access is not a barrier. Health Canada just wants to see that its done in a regulated manner.”

 People are “incredibly naive” about the kinds of drugs and treatments that are out there, he says. At the same time, he worries access to these drugs would open up what he calls the “Wild West.” Vulnerable patients could be at the mercy of drug companies selling potions they know don’t work, he argues. Drug companies could charge whatever they want, and families would be on the hook for debts caused by experimental treatments, even if the patient dies.